Featured series 
Tag: gene therapy
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Health
Gene-editing treatment could replace cholesterol meds
Early stage test shows promise, but cardiologist notes more study needed into longer-term, unintended effects
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Campus & Community
Veteran biotech executive to run new center aimed at boosting cell and gene therapies
Landmark Bio, a new center for advanced cell manufacturing, announced that former Orchard Therapeutics, Amgen, and Genzyme executive Ran Zheng will take over as chief executive. Landmark Bio is a partnership of Boston-area universities, hospitals, and private industry led by Harvard and MIT.
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Campus & Community
Big step forward for planned center to boost cell- and gene-therapy advances
A new cell manufacturing and innovation center, headed by a unique partnership between academia and industry, has taken a key step — signing a lease in Watertown for its new home — as it looks toward 2022 opening.
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Health
Power and pitfalls of gene editing
CRISPR gene-editing technology has conquered the lab and is poised to lead to new treatments for human disease. Experts consider the promise and peril at Radcliffe.
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Health
Gene therapy was a ‘last shot’
Three years after undergoing gene therapy at Dana-Farber/Boston Children’s Cancer and Blood Disorders Center to treat a life-threatening immune disorder, an Ohio college student is no longer thinking about his own “last shot” for health, but rather about medical school and “giving back.”
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Health
Finally, hope for a young patient
A gene therapy trial points to a healthier future for a young patient suffering from a rare immune disease.
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Health
New hope in old viruses
Harvard Stem Cell Institute researchers at Massachusetts Eye and Ear have reconstructed an ancient virus that is highly effective at delivering gene therapies to the liver, muscle, and retina.
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Health
‘Bubble boy’ gene therapy raises hope
A new form of gene therapy for boys with the life-threatening condition known as “bubble boy” disease appears to be both effective and safe, according to an international clinical trial run by a team from Harvard Medical School, Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, and other institutions.
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Health
A shot against heart attacks?
Harvard Stem Cell Institute scientists collaborating with researchers at the University of Pennsylvania have developed a “genome-editing” approach for permanently reducing cholesterol levels in mice through a single injection, a development with the potential to reduce the risk of heart attacks in humans by 40 to 90 percent.
