Tag: SMA

  • Nation & World

    Compound protects nerve cells targeted by diseases

    Harvard researchers have identified a compound that helps protect the cells destroyed by spinal muscular atrophy, the most frequent fatal genetic disease of young children.

    5 minutes
  • Nation & World

    Hope against disease targeting children

    Harvard Stem Cell Institute researchers studying spinal muscular atrophy have found molecular changes that help trigger the genetic disease in children.

    4 minutes
  • Nation & World

    Link found between ALS and SMA

    Scientists have long known the main proteins that lead to the development of amyotrophic lateral sclerosis (ALS) and spinal muscular atrophy (SMA), respectively. Now research shows that these two motor neuron diseases likely share a pathway that leads to the development of disease.

    3 minutes
  • Nation & World

    From skin cells to motor neurons

    Harvard stem cell researchers have succeeded in reprogramming adult mouse skin cells directly into the type of motor neurons damaged in amyotrophic lateral sclerosis, best known as Lou Gehrig’s disease, and spinal muscular atrophy.

    4 minutes